For the first time in his life, a young New Jersey man is pain-free thanks to a new gene treatment working to cure patients ...

Researchers found a small molecule that increases fetal hemoglobin ... providing proof of principle for developing more effective therapeutics for sickle cell disease. Sickle cell disease, while ...

Its been a rough and tumble 2022 for Editas Medicine, marked by a new executive team, the suspension of its lead asset and navigating a clinical hold on the efficacy portion of a sickle cell program.

At age 45, Dr. Lakiea Bailey said, she was the oldest person with sickle cell anemia that she knew ... It also noted the study’s small size. In a discussion of the company’s methodology ...

As a result, sickle cell experts said, only a small fraction of patients in the United States are expected to receive the new treatment (to say nothing of the millions of sickle cell patients ...

When Patricia McGill was 13 and learning that she had inherited sickle cell disease ... It causes red blood cells to “get stuck in small blood vessels, leading to painful crises, inflammation ...