Independent Record8h
'The Life of Riley': Helena mother's book chronicles family's battle with Duchenne muscular dystrophy
Despite the obstacles, Riley Herrera had a life filled with family, sports, travel, faith and hope before his death on Nov.
How a teen living with muscular dystrophy helps raise funds for Holland Bloorview
At just 15 years old, Ragheeb has already made a tremendous impact on his community as an ambassador for Capes for Kids, an ...
Sunday World7h
Boy (7) with rare condition flies to US for testing as ‘not enough’ treatment in Ireland
A seven-year-old boy from Dublin is on his way to California to undergo testing after being diagnosed with a rare condition last year.
KCLR96FM10h
A Kilkenny family is on a mission to raise €4 million to save their 4-year-old son’s life
A Kilkenny family is urgently raising €4 million euro for life-saving treatment for their 4-year-old son. William Jonathan Moore, who was diagnosed with Duchenne Muscular Dystrophy (DMD) in 2024.
biopharma-reporter8d
Roche’s Elevidys demonstrates significant benefits for DMD patients in Phase 3
The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...
Managed Healthcare Executive13d
FDA and EMA Accepts Applications for New Nusinersen Regimen
An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...