How a teen living with muscular dystrophy helps raise funds for Holland Bloorview
At just 15 years old, Ragheeb has already made a tremendous impact on his community as an ambassador for Capes for Kids, an ...
Independent Record12h
'The Life of Riley': Helena mother's book chronicles family's battle with Duchenne muscular dystrophy
Despite the obstacles, Riley Herrera had a life filled with family, sports, travel, faith and hope before his death on Nov.
Sunday World11h
Boy (7) with rare condition flies to US for testing as ‘not enough’ treatment in Ireland
A seven-year-old boy from Dublin is on his way to California to undergo testing after being diagnosed with a rare condition last year.
charitytoday.co.uk1d
Call for people with muscle conditions to join support group
Tony, from Skellingthorpe, Lincoln, was diagnosed with myofibrillar myositis and anti-SRP immune-mediated necrotizing ...
biopharma-reporter8d
Roche’s Elevidys demonstrates significant benefits for DMD patients in Phase 3
The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...
Managed Healthcare Executive13d
FDA and EMA Accepts Applications for New Nusinersen Regimen
An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...
PMLiVE8d
Roche/Sarepta announce two-year results for Duchenne muscular dystrophy gene therapy
Roche and Sarepta Therapeutics have shared positive top-line results from a late-stage study of Elevidys (delandistrogene ...