Until the first drug for SMA arrived in 2016, children typically died before age 2 ... JON HAMILTON, BYLINE: Doug McCullough ...

Study using a new, child-friendly scale found patients up to age 2 had smaller mouth openings than healthy peers, risking ...

Three people with a muscle-destroying disease destined to worsen got a little stronger when an implanted device zapped their ...

In surveys, parents of children with SMA and healthcare professionals in Sweden note the many ways the pandemic affected ...

An experimental treatment that stimulates the spinal cord may help people with a paralyzing genetic disorder called spinal muscular atrophy.

How a tiny spinal implant could help those with muscle-wasting disease - Three people with a muscle-destroying disease got ...

An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...

Jayceon Jackson was full of smiles as his parents pushed his wheelchair into Nationwide Children’s Hospital, Wednesday. It was Jayceon’s birthday wish for people to gift him teddy bears so he could ...

A Boston-area biopharmaceutical firm has submitted a biologics license application to the FDA for its investigational, fully ...

In a small human trial in SMA patients neurostimulation sessions improved motoneuron function, reduced fatigue, and improved leg muscle strength and walking.

Electrical stimulation of the spinal cord strengthened the muscles of three people with spinal muscular atrophy, a rare motor neuron disease.