For centuries, hemophilia was a dangerous genetic disorder with no treatment. Children with hemophilia often didn't make it to adulthood, since a bump or fall could cause massive internal bleeding.
Hemophilia B is a genetic disorder that affects how well the blood clots. Treatment involves supplementing the factor IX protein, but new therapies may offer alternative ways to manage factor IX ...
The subcutaneous injection drug emicizumab (Hemlibra), for instance, greatly reduces bleeding in hemophilia A, the most common form of this bleeding disorder. Ben Samelson-Jones, MD, PhD “It’s ...
UC San Diego announced that it is offering a newly Food and Drug Administration-approved gene therapy for hemophilia B, a ...
The results, which were recently published in the journal Blood, contribute significantly to a better understanding of the disease. Hemophilia is a hereditary blood disorder characterized by a ...
A recent study led by MedUni Vienna provides new insights into the mechanisms of coagulation in persons with hemophilia A ... a better understanding of the disease. Haemophilia is a hereditary ...
Financial writer discusses MGX's gene editing technology, cash runway, and lack of clinical data for potential future ...
Hemlibra was found to ease pain and improve quality of life for hemophilia A patients, even those with long-term joint damage, per a study.