Biogen has announced that the European Medicines Agency (EMA) and US Food and Drug Administration (FDA) have started ...

Problems with chemical messengers like dopamine were tied to posture issues in SMA in a mouse study, but levodopa therapy may ease symptoms.

The Muscular Dystrophy Association (MDA) has selected Lily Sander from Charlotte, North Carolina, as its 2025 MDA National ...

Progressive Muscular Atrophy, Spinal Macular Atrophy Kennedy's disease, and Post-polio Syndrome," said Dr Wendo. Messages or signals from nerve cells in the brain's upper motor neurons are ...

The health activists argue that the government is empowered with effective law and policy tools and therefore should ...

Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...

A woman with SMA type 3 became pregnant while on Spinraza treatment and gave birth to a healthy child, per a case report.

Five more rare diseases have been identified in the country, making the total number of rare diseases reach 456, according to ...

Health activists demand government action to reduce the cost of SMA medicines, citing constitutional obligations and ...

An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...

A man with a muscle-wasting disease is pleased Manitoba is asking a federal agency to reconsider its opposition to a ...