The parents of two-year-old Aakriti Singh diagnosed with Spinal Muscular Atrophy – SMA type-1, are worried about her next ...

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More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...

A man with a muscle-wasting disease is pleased Manitoba is asking a federal agency to reconsider its opposition to a ...

Patients with spinal muscular atrophy (SMA) type 2 showed improved motor ability when treated with intrathecal onasemnogene ...

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...

For children with SMA, assistive devices -- walkers, wheelchairs, standers, and more -- are the key to staying active. Learn which ones may help your child.

Topline results of a phase 3 clinical trial of an investigational gene therapy for spinal muscular atrophy type 2 found the treatment ... on data from the phase 1/2 open-label STRONG clinical ...

was the first potential cure for babies with spinal muscular atrophy. The new medicine would be administered differently and target older children. When introduced, Zolgensma was priced at $2.1 ...