Muscular Dystrophy News4h
Boys with DMD given Elevidys 2 years ago still showing motor gains
Top-line Phase 3 trial data show ambulatory boys with Duchenne continued with motor improvements two years after a single ...
TooFab2d
Leah Messer Reveals Parenting 'Challenge' with Daughter's Muscular Dystrophy
The Next Chapter star Leah Messer opens up about navigating protecting her daughter Ali amid her muscular dystrophy diagnosis ...
Pop Culture2d
‘Teen Mom’s Leah Messer Calls Navigating Daughter Ali’s Muscular Dystrophy ‘Very Challenging’ as She Hits High School (Exclusive)
Teen Mom star Leah Messer admits it’s “very challenging” helping daughter Aliannah “balance” her desire for freedom with the ...
biopharma-reporter1d
Roche’s Elevidys demonstrates significant benefits for DMD patients in Phase 3
The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...
Muscular Dystrophy Association Announces 2025 MDA National Ambassador Lily Sander
The Muscular Dystrophy Association (MDA) has selected Lily Sander from Charlotte, North Carolina, as its 2025 MDA National ...
PMLiVE1d
Roche/Sarepta announce two-year results for Duchenne muscular dystrophy gene therapy
Roche and Sarepta Therapeutics have shared positive top-line results from a late-stage study of Elevidys (delandistrogene ...
Gulf Times22h
Sidra Medicine establishes gene therapy centre for rare paediatric diseases
Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...
Managed Healthcare Executive5d
FDA and EMA Accepts Applications for New Nusinersen Regimen
An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...