For the first time in his life, a young New Jersey man is pain-free thanks to a new gene treatment working to cure patients ...

Researchers found a small molecule that increases fetal hemoglobin ... providing proof of principle for developing more effective therapeutics for sickle cell disease. Sickle cell disease, while ...

When asked to picture the ideal cure for sickle-cell disease, molecular biologist ... but can be packaged as small molecules,” Thompson says. Notably, both Rivella and Thompson stress that ...

Its been a rough and tumble 2022 for Editas Medicine, marked by a new executive team, the suspension of its lead asset and navigating a clinical hold on the efficacy portion of a sickle cell program.

including small costs that can add up quickly, like transportation and parking. Tens of thousands of lower-income families with children suffering from sickle cell disease have applied for the ...

I became an advocate for sickle cell and learned the skills to become a journalist. The seemingly small act of donating blood has a lasting impact on those in need. It has strengthened me so that ...

As a result, sickle cell experts said, only a small fraction of patients in the United States are expected to receive the new treatment (to say nothing of the millions of sickle cell patients ...

At age 45, Dr. Lakiea Bailey said, she was the oldest person with sickle cell anemia that she knew ... It also noted the study’s small size. In a discussion of the company’s methodology ...