The Muscular Dystrophy Association (MDA) has selected Lily Sander from Charlotte, North Carolina, as its 2025 MDA National ...

The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...

In year two of the trial, Elevidys demonstrated statistically significant and clinically improvements across three key ...

While the last decade has brought considerable progress for patients with DMD, substantial unmet need remains. Several ...

Roche and Sarepta Therapeutics have shared positive top-line results from a late-stage study of Elevidys (delandistrogene ...

Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...

MDA launches 75th Anniversary campaign and premieres new public service announcement (PSA) to mark 75 years of impact in the ...

The announcement was made at Arab Health 2025 where Sidra Medicine will highlight its international patient service programmes ...

The various types of MD affect more than 50,000 Americans. Through advances in medical care, children with muscular dystrophy are living longer than ever before. Muscular dystrophy is caused by ...

Executive director and ‘chief energy officer’ brings positivity, servant leader mentality to David’s Refuge, a nonprofit ...

For Captain Joe Dion, it’s about caring for his family. The 38-year-old father of three took two seasons off from the job ...

Duchenne muscular dystrophy (DMD) is the most common type ... and symptoms usually begin early in childhood. Children with DMD have a hard time standing up, walking, and climbing stairs.