Gateshead teenager first in the UK to be recruited to heart failure trial after family's 'double blow'
Robert Davidson is the first UK patient recruited to a new medical trial looking to support children with heart failure ...
How a teen living with muscular dystrophy helps raise funds for Holland Bloorview
At just 15 years old, Ragheeb has already made a tremendous impact on his community as an ambassador for Capes for Kids, an ...
Independent Record1d
'The Life of Riley': Helena mother's book chronicles family's battle with Duchenne muscular dystrophy
Despite the obstacles, Riley Herrera had a life filled with family, sports, travel, faith and hope before his death on Nov.
Muscular Dystrophy News6d
To a parent, the years always seem too short
Columnist Betty Vertin has learned that as a parent, she's finding the years with all her children, including those with DMD, too short.
Sunday World1d
Boy (7) with rare condition flies to US for testing as ‘not enough’ treatment in Ireland
A seven-year-old boy from Dublin is on his way to California to undergo testing after being diagnosed with a rare condition last year.
charitytoday.co.uk2d
Call for people with muscle conditions to join support group
Tony, from Skellingthorpe, Lincoln, was diagnosed with myofibrillar myositis and anti-SRP immune-mediated necrotizing ...
biopharma-reporter9d
Roche’s Elevidys demonstrates significant benefits for DMD patients in Phase 3
The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...
PMLiVE9d
Roche/Sarepta announce two-year results for Duchenne muscular dystrophy gene therapy
Roche and Sarepta Therapeutics have shared positive top-line results from a late-stage study of Elevidys (delandistrogene ...
Gulf Times9d
Sidra Medicine establishes gene therapy centre for rare paediatric diseases
Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...