Abu Dhabi (DoH), the regulator of the healthcare sector in the Emirate, M42, a global health champion powered by AI, technology and genomics and PureHealth, the largest healthcare group in the Middle ...

The Syrian girl suffers from spinal muscular atrophy, a rare and serious genetic disorder that affects muscle strength and ...

Roche's Evrysdi has already shown profound benefits in children with spinal muscular atrophy (SMA) given after birth – but doctors in the US believe treatment should start even before that.

A new neonatal screening test recently saved the life of a little girl with spinal muscular atrophy, a rare neuromuscular ...

Roughly 53 million people in the U.S. provide care to a family member such as a child with complex medical needs, an aging ...

The family of Yaqeen Ibrahim Kanaker, a Syrian child, confirmed that she began treatment on Thursday at Al Jalila Children's ...

Panelists discuss how gaps in SMA care persist despite highly effective treatments, particularly regarding racial and ethnic disparities in research participation and global access challenges due to ...

With more than 2,100 members, EMBO stands for excellence in the life sciences. It accepts outstanding researchers who are ...

Treatment with salanersen slowed neurodegeneration and improved motor function in children with SMA in a Phase 1 trial, ...

Sheikh Mohammed bin Rashid funds Dh7 million treatment for a young Syrian girl with spinal muscular atrophy, giving her a ...