Genetic mutations in many forms of ALS lead to early problems with the transport and function of mitochondria, a study found.

Learn how a new genetic therapy could transform treatment for rare ALS—keep reading for remarkable patient outcomes.

Typically, the goal of ALS treatments is to slow the disease or halt progression. But new data from the antisense oligonucleotide (ASO) jacifusen for FUS-ALS show that two patients went beyond the ...

Experimental drug Ulefnersen shows potential in halting and even reversing symptoms in patients with FUS- Amyotrophic lateral ...

163.com Conclusions These findings demonstrated that the genetic architecture of ALS in Asian populations is distinct from that in European populations, which need to be given appropriate ...

Some patients with a rare form of ALS benefited from an experimental therapy, with biomarker evidence of reduced injury to neurons and even limited functional recovery.

The Met’s selection—from a private collection amassed by the American photography dealer William L. Schaeffer, and now a ...

John Driskell Hopkins has lived with ALS for three and a half years. The Zac Brown Band musician updates us and shares a new song for his daughters.

An experimental drug known as ulefnersen has shown remarkable efficacy in treating a rare, aggressive form of ALS ...

When Columbia neurologist and scientist Neil Shneider speaks to his ALS patients who volunteer for experimental therapies, he ...

An experimental drug could help young people with a rare form of ALS, researchers at New York’s Columbia University Irving ...

Nearly doubled quality of life for users Like the study in Sweden, the German research shows that overall quality of life is almost doubled among users with a communication aid, compared to how life ...