I may be the last person on earth to be personally confronted by the potential of AI technology. I knew it would come for our ...

A study published today in the journal Cell marks the first reported instance of generative AI designing synthetic molecules that can successfully control gene expression in healthy mammalian cells.

Data contribute to growing body of support around the anti-fibrotic activity of EFX in patients with pre-cirrhotic MASH SOUTH SAN FRANCISCO, Calif., May 10, 2025 (GLOBE NEWSWIRE) -- Akero Therapeutics ...

For example, the FDA-oriented primary endpoint in hemophilia gene therapy trials is a laboratory measure of coagulation factor activity. So, BioMarin has included as a secondary endpoint ...