Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for Priority Review to be given. Explore more details here.

A man with a muscle-wasting disease is pleased Manitoba is asking a federal agency to reconsider its opposition to a ...

Find Spinal Muscular Atrophy Sma Latest News, Videos & Pictures on Spinal Muscular Atrophy Sma and see latest updates, news, information from NDTV.COM. Explore more on Spinal Muscular Atrophy Sma .

Biogen has announced that the European Medicines Agency (EMA) and US Food and Drug Administration (FDA) have started ...

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Scholar Rock (SRRK), a late-stage biopharmaceutical company developing innovative treatments for spinal muscular atrophy, ...

Health activists demand government action to reduce the cost of SMA medicines, citing constitutional obligations and ...

An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...

The health activists argue that the government is empowered with effective law and policy tools and therefore should ...

There is no cure for spinal muscular atrophy, but treatments can stop its progression and often lead to some improvement. However, Manitoba has refused to pay for the hugely expensive treatment ...