Age affects every type of body tissue, including skin, muscles, bone, and more. Learn about the specific effects of aging on ...

The European Commission approved a tablet formulation of SMA treatment Evrysdi, a form aimed at giving patients more ...

Panelists discuss how disease progression despite treatment in older patients with spinal muscular atrophy (SMA) may be due to natural aging effects combined with SMA, not necessarily treatment ...

dvm360 connects veterinarians to essential medical news, veterinary expertise, and insights on pet care products and ...

Dr. Tejal Aslesh Tailor is an accomplished neuroscientist and molecular biologist with years of expertise in preclinical ...

MRI imaging scans can track muscle changes in SMA children given Spinraza, a study found, with better results seen with early ...

and much-needed therapeutic option for patients living with SBMA—a disease that currently lacks any FDA-approved treatments.” "AnnJi reports outcomes from trial of spinal bulbar muscular atrophy ...

22. Apitegromab is an investigational treatment aimed at improving motor function for people living with spinal muscular atrophy. Scholar Rock said it has also submitted and received validation ...

05. Nearly six years ago, the Food and Drug Administration approved Zolgensma, a Novartis gene therapy for the fatal neuron-wasting disease spinal muscular atrophy. It heralded a new era of ...

In a hopeful step for medicine, a 2-and-a-half-year-old child born with spinal muscular atrophy (SMA) has shown no symptoms ... case of prenatal therapy that holds promise for future treatment of the ...

The first prenatal treatment for spinal muscular atrophy showed promise in a single case report. Risdiplam was given to the mother during pregnancy and to the child after birth. More than 2 years ...

There is no cure for spinal muscular atrophy, but treatments can stop its progression and often lead to some improvement. However, Manitoba has refused to pay for the hugely expensive treatment ...