Patient advocate Austin Leclaire, who died Feb. 1, played a pivotal role in spurring the development of the first medicines ...

The symptoms of myotonic dystrophy may be obvious from birth or they can develop later -- during the teenage or adult years. Like other forms of muscular dystrophy, myotonic dystrophy leads to ...

Duchenne muscular dystrophy (DMD) is the most common type ... They should see a cardiologist in their late teens or early adult years to check for any problem. Some blood pressure medicines ...

Robert Davidson is the first UK patient recruited to a new medical trial looking to support children with heart failure ...

A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and ...

Contrary to prior data, this study shows that neither eosinophils nor STAT6-mediated IL-4/IL-13 signaling contribute ...

Entrada plans to initiate clinical testing of ENTR-601-44 in Duchenne MD patients amenable to exon 44 skipping later this year.

Tony, from Skellingthorpe, Lincoln, was diagnosed with myofibrillar myositis and anti-SRP immune-mediated necrotizing ...