Three people with a muscle-destroying disease destined to worsen got a little stronger when an implanted device zapped their ...
A new spinal cord implant may help people with spinal muscular atrophy (SMA) regain some muscle function, giving the ...
In a small human trial in SMA patients neurostimulation sessions improved motoneuron function, reduced fatigue, and improved leg muscle strength and walking.
How a tiny spinal implant could help those with muscle-wasting disease - Three people with a muscle-destroying disease got ...
A Boston-area biopharmaceutical firm has submitted a biologics license application to the FDA for its investigational, fully ...
while the rest comprise of medicines to treat rare diseases including spinal muscular atrophy (SMA), among others. Union finance minister Nirmala Sitharaman has proposed exempting 36 life saving drugs ...
Study using a new, child-friendly scale found patients up to age 2 had smaller mouth openings than healthy peers, risking ...
Evrysdi is the third treatment approved for SMA, an ultra-rare muscle wasting disease that can begin in early childhood, after Biogen’s Spinraza (nusinersen) and Novartis’ Zolgensma ...
SMA is a rare and often fatal genetic disease that causes muscle weakness and progressive loss of movement. Approximately 550 to 600 infants are born with SMA in Europe each year. Now, the CHMP ...