Whether you are a competitive athlete or an older adult, strong bones are essential—not only for movement, but also for ...

New gene therapy improves the life of 18-year-old with Sickle Cell Disease which affects 5,000 New Jersey residents living ...

Sanofi's rilzabrutinib earns its fourth orphan drug status from the FDA, this time targeting sickle cell disease.

Researchers have discovered a breakthrough link between organ failure and long Covid after overcoming contentious Covid-era ...

Paris: Sanofi has received orphan drug designation from the US Food and Drug Administration (FDA) for rilzabrutinib, a novel, ...

According to reports, an estimated 7.74 million people lived with sickle cell disease in 2021. Sickle cell anaemia can be a ...

An algorithm is helping to reduce the number of unnecessary hospital admissions for children with sickle cell.

Scientists at the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Milan, have found that gene editing using ...

"Sickle cell disease is a devasting disorder that affects approximately 100,000 people in the U.S., leading to anemia, severe ...

Rilzabrutinib granted orphan drug designation in the US for sickle cell disease <li /> Fourth orphan drug designation for rilzabrutinib ...

Northwestern Medicine scientists have uncovered new details about how poxvirus hijacks its host's protein synthesis machinery ...