PMLiVE1d
Biogen’s higher dose spinal muscular atrophy regimen accepted for review by EMA/FDA
Biogen has announced that the European Medicines Agency (EMA) and US Food and Drug Administration (FDA) have started ...
Gulf Times1d
Sidra Medicine establishes gene therapy centre for rare paediatric diseases
Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...
Managed Healthcare Executive6d
FDA and EMA Accepts Applications for New Nusinersen Regimen
An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...
Qatar Tribune on MSN1d
Qatar: Sidra establishes Gene Therapy Center for rare genetic diseases
The announcement was made at Arab Health 2025 where Sidra Medicine will highlight its international patient service programmes ...
standardmedia.co.ke3d
Battle against the body's own nerves: How Motor Neurone Disease alters lives
MNDs are neurological disorders that destroy motor neurons, the cells that control skeletal muscle activity such as walking, breathing, speaking, and swallowing.
SMA23h
Levodopa therapy could ease SMA symptoms, per new mouse study
Problems with chemical messengers like dopamine were tied to posture issues in SMA in a mouse study, but levodopa therapy may ease symptoms.
SMA3d
Spinal cord gray matter may be imaging marker of SMA types 2, 3
More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...
Zacks.com on MSN21h
Biotech Stock Roundup: SAGE Up on Declining BIIB's Offer, CYTK, AKRO Up on Updates
It was a busy week for the biotech sector, with regulatory and pipeline updates. Sage Therapeutics SAGE was in focus after it ...
verywellhealth6d
Brain Tumors
It is used to diagnose neurological conditions such as a brain tumor, Parkinson’s disease, multiple sclerosis (MS), and spinal muscular atrophy. The Neurological ... What are the symptoms of a brain ...