Michael Gehr, of Edmond, and his family are on a mission to help find a cure for a rare genetic disease that he was diagnosed ...

Qureight, a deep-learning analytics company accelerating drug development through AI-powered data curation, today announced that its digitally-twinned synthetic control arm has been used in a ...

Trump health officials signal eased FDA rules for rare disease gene therapy, but concerns linger over safety, oversight, and ...

FT Island member Lee Hong-ki confessed to the pain of a rare disease that he has suffered for nearly 20 years, causing ...

FTISLAND’s Lee Hong Gi has shed light on his painful, decades-long fight with a rare chronic illness. On the June 15th ...

Cruz, who turned 18 on Tuesday, has a rare genetic disease called neurofibromatosis type 1 (NF1) that causes tumors to grow all over his body. He shared his story last week with members of Congress as ...

Guest Opinion. The path forward for rare disease patients and their families historically has been rocky, littered with ...

The illness is caused by a parasite, which makes it different from many well-known tick-borne diseases, such as Lyme.

Cancer incidence rates among members of Generation X were two to three times higher than among people born in the 1940s, ...

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Eddie Vedder and wife Jill share why they’ve become so involved in awareness for a rare disease in an exclusive clip from new film 'Matter of Time' ...