News

Newborn screening is also cost-effective. Testing that takes just a few dollars per baby can save families and the health ...
Families say it's 'completely frustrating' that children with Duchenne Muscular Dystrophy are being denied access to free ...
Michael Rankin, 12, who is desperately waiting for access to the drug, said: “Every second they don’t get this through, one ...
Duchenne Muscular Dystrophy: diagnosis, clinical development and global researchMuscular dystrophy refers to a group of rare, genetic, progressive diseases that primarily affect the body’s muscles, ...
Patients in Scotland can't get the treatment - which is available in England - despite manufacturers giving it away for free to the NHS.
John Brandsema, MD, a pediatric neurologist at Children’s Hospital of Philadelphia, speaks with Healio about the importance of early diagnosis of muscular dystrophy.
John Brandsema, MD, a pediatric neurologist at Children’s Hospital of Philadelphia, speaks with Healio about the current understanding of the genetic factors behind muscular dystrophy.
Scientists found a genetic link between autism and DM1, where repeat DNA sequences disrupt brain gene splicing. This sheds ...
Children with a rare form of muscular dystrophy have been promised access to a groundbreaking drug after the Sunday Mail highlighted their plight. Around 30 boys could have their lives extended by ...
The NHS has rolled out a new treatment for muscular degeneration at a few sites in England and Wales, while Scotland and Northern Ireland do not have access. | ITV National News ...