News

A new neonatal screening test recently saved the life of a little girl with spinal muscular atrophy, a rare neuromuscular ...
Abu Dhabi (DoH), the regulator of the healthcare sector in the Emirate, M42, a global health champion powered by AI, technology and genomics and PureHealth, the largest healthcare group in the Middle ...
Sheikh Mohammed bin Rashid funds Dh7 million treatment for a young Syrian girl with spinal muscular atrophy, giving her a ...
The family of Yaqeen Ibrahim Kanaker, a Syrian child, confirmed that she began treatment on Thursday at Al Jalila Children's ...
The ruler of Dubai, His Highness Sheikh Mohammed bin Rashid Al Maktoum, has covered the cost of Syrian girl Yaqeen Ibrahim ...
The Syrian girl suffers from spinal muscular atrophy, a rare and serious genetic disorder that affects muscle strength and ...
Roughly 53 million people in the U.S. provide care to a family member such as a child with complex medical needs, an aging ...
Spinal Muscular Atrophy known as SMA is a rare genetic disease that affects 1 in 6,000 children. And, tonight, the parents of 6 month old baby Emiliano Flores are calling out for help for their son.
Treatment with salanersen slowed neurodegeneration and improved motor function in children with SMA in a Phase 1 trial, ...
Baby Aasmika with SMA Type 1 received Zolgensma, the world’s most expensive gene therapy, thanks to India's largest-ever ...
A survey found that people give more frequently to organisations they trust are reliable and use funds wisely. Read more at ...
New analyses from DEVOTE Part C further characterize the improvements in motor function in participants with SMA who transitioned to the investigational higher dose regimen of nusinersen from 12 mg SP ...