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MED-EL USA, a pioneer in hearing implant technology, today announced that new and existing MED-EL hearing implant recipients can access a year of the Meludia online music training program at no cost.

Biogen has announced that the European Medicines Agency (EMA) and US Food and Drug Administration (FDA) have started ...

The announcement was made at Arab Health 2025 where Sidra Medicine will highlight its international patient service programmes ...

Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...

Roche has reported positive results from the second year of the EMBARK Phase III trial of Elevidys (delandistrogene moxeparvovec), the first approv ...

MNDs are neurological disorders that destroy motor neurons, the cells that control skeletal muscle activity such as walking, breathing, speaking, and swallowing.

Thiruvananthapuram: The Kerala government is planning to launch a registry for rare diseases and set up a treatment clinic in ...

Thiruvananthapuram, A registry for rare disease patients in the state will become a reality this year, State Health Minister ...

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...