Genetic mutations in many forms of ALS lead to early problems with the transport and function of mitochondria, a study found.

Some patients with a rare form of ALS benefited from an experimental therapy, with biomarker evidence of reduced injury to neurons and even limited functional recovery.

Treatment with an experimental drug has shown significant improvements in young patients with a rare form of Amyotrophic ...

Data from 12 patients – all treated with a novel therapy for a rare form of ALS caused by a genetic mutation in a gene called ...

An experimental drug known as ulefnersen has shown remarkable efficacy in treating a rare, aggressive form of ALS ...

Experimental drug Ulefnersen offers hope for rare, early-onset Amyotrophic lateral sclerosis (ALS) in clinical trials.

Typically, the goal of ALS treatments is to slow the disease or halt progression. But new data from the antisense oligonucleotide (ASO) jacifusen for FUS-ALS show that two patients went beyond the ...

When Columbia neurologist and scientist Neil Shneider speaks to his ALS patients who volunteer for experimental therapies, he ...

Learn how a new genetic therapy could transform treatment for rare ALS—keep reading for remarkable patient outcomes.

Grant terminations at Harvard have affected research on antibiotic resistance, identifying the earliest precursors of breast cancer and finding cures for ALS.

John Driskell Hopkins has lived with ALS for three and a half years. The Zac Brown Band musician updates us and shares a new song for his daughters.