Microglia replacement therapy helps treat people with a rare genetic condition called ALSP, suggesting the approach could ...

The U.S. Food and Drug Administration has declined to approve Ultragenyx Pharmaceutical's experimental gene therapy to treat ...

In a paper published last month, researchers at UT Southwestern Medical Center introduced lipid nanoparticles — hollow, fatty ...

With the initiative, families can have their baby’s full genetic code sequenced at no cost to identify potentially serious ...

Gov. Ron DeSantis last month signed the law (HB 907), which was unanimously passed by the Legislature in April and is dubbed ...

Researchers from the University of Adelaide are hopeful a recent biological discovery could lead to the precision treatment ...

For decades, the dream of fixing harmful mutations in mitochondrial DNA felt out of reach. Scientists have long known these ...

Penn Medicine researchers have identified genetic conditions in a large percent of adults admitted to the intensive care unit ...

As predicted the era of universal newborn genomic screening is dawning. The UK and Florida are leading the way.

Wondering if autism is inherited Read ahead to know what the science and experts say about autism genetics and why the ...

Charlie Health reports that eating disorders are significantly influenced by genetics, with family history increasing risk dramatically.

A woman with a rare genetic disorder called Apert syndrome turned an ordinary treadmill run into an extraordinary 26.2-mile feat. She documented it on TikTok and it went viral.