More information: Ulrike M. Reiss et al, Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia B, New England Journal of Medicine (2025). DOI: 10.1056/NEJMoa2414783 ...

Discovery could improve treatment for people with hemophilia A by Centenary Institute edited by Sadie Harley, reviewed by Robert Egan Editors' notes ... Credit: CC0 Public Domain ...

Hemophilia A follows an X-linked recessive inheritance pattern, meaning the altered gene resides on the X chromosome. This genetic arrangement explains several characteristic patterns observed in ...

Hemophilia significantly impacts lives beyond bleeding episodes, causing absenteeism, pain, and disability. India, with the second-highest hemophilia population, faces challenges in diagnosis and ...

World Hemophilia Day has been observed every year since 1989, thanks to the efforts of the World Federation of Hemophilia (WFH). The day was chosen in honor of Frank Schnabel, the founder of WFH ...

Hemophilia is a bleeding disorder. Every year April 17 is marked as World Hemophilia Day. The psychological journey of living with hemophilia is often as challenging as the physical one. Uncover ...

March 31, 2025 – The FDA has approved a new drug as a preventive treatment to reduce bleeding episodes in people with certain types of hemophilia. This first-of-its-kind injectable drug offers a ...

Qfitlia’s efficacy and safety were assessed in two multicenter, randomized clinical trials which enrolled a total of 177 adult and pediatric male patients with either hemophilia A or hemophilia B.

Over the last three years, the FDA has approved six new hemophilia drugs, including three gene therapies. | Over the last three years, the FDA has approved six new drugs for hemophilia. And now ...

Pfizer’s experience mirrors the struggles of other hemophilia gene therapy players. CSL’s first-to-market rival hemophilia B gene therapy, Hemgenix, has also faced a slower-than-expected launch.

For centuries, hemophilia was a dangerous genetic disorder with no treatment. Children with hemophilia often didn't make it to adulthood, since a bump or fall could cause massive internal bleeding.

DelveInsight's Hemophilia A Market report offers an in-depth understanding of the epidemiology and market trends in the 7MM. LAS VEGAS, NV, UNITED STATES, January 13, 2025 /EINPresswire ...