FDA-approved treatments for spinal muscular atrophy differ in their mechanisms of action, safety profiles, and administration ...

Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...

However, this type of atrophy is reversible with regular exercise and physical therapy. People can treat muscle atrophy by making lifestyle changes, trying physical therapy, or undergoing surgery.

The NIH is considering a catastrophic cut to indirect cost reimbursements for public universities, which would hurt the ...

You're in what they call the ‘golden years’ of life — your children are well-settled, you live comfortably, and have saved ...

DMD was first described by French neurologist Guillaume Benjamin Amand Duchenne in the 1860s. However, until the 1980s, ...

Funding medical research is about more than just numbers. It's real people,” says Ryan Manriquez, president of the UC ...

Scholar Rock (SRRK) announced that the U.S. Food and Drug Administration FDA has accepted its Biologics License Application BLA for ...

It's that time of year when you can become a Hero for Hope and donate to ABC15's annual Telethon for Phoenix Children's ...

Children with SMA in the U.K. can switch treatments based on practical needs and preferences without unexpected disease ...