Simplified storage and administration of new tablet formulation may provide greater freedom and independence for people with ...

Roche’s Evrysdi (risdiplam) tablets have been approved by the European Commission (EC) to treat spinal muscular atrophy (SMA) ...

Panelists discuss how disease progression despite treatment in older patients with spinal muscular atrophy (SMA) may be due to natural aging effects combined with SMA, not necessarily treatment ...

European Commission approves Roche’s Evrysdi tablet to treat spinal muscular atrophy: Basel Thursday, June 5, 2025, 09:00 Hrs [IST] Roche announced that the European Commission ...

dvm360 connects veterinarians to essential medical news, veterinary expertise, and insights on pet care products and ...

Basel: Roche has announced that the European Commission (EC) has approved a label extension for Evrysdi (risdiplam) to ...

Subjects receiving the therapy demonstrated clinically meaningful enhancements in physical and muscle function.

Dr. Tejal Aslesh Tailor is an accomplished neuroscientist and molecular biologist with years of expertise in preclinical ...

Panelists discuss how supportive care for patients with spinal muscular atrophy (SMA) includes rehabilitation, respiratory ...

Rainbow Children’s Hospital, a leading chain of hospitals for paediatric, obstetrics and gynaecology, successfully administered gene therapy to a child diagnosed with Spinal Muscular Atrophy (SMA) at ...

In the first part of this series, we explored how early genetic screening and gene therapy transform the lives of newborns ...

Researchers have taken preliminary steps toward treating a devastating neurodevelopmental disorder, spinal muscular atrophy ... the earlier treatment can start, the better the outcome.