Patient advocate Austin Leclaire, who died Feb. 1, played a pivotal role in spurring the development of the first medicines ...

Contrary to prior data, this study shows that neither eosinophils nor STAT6-mediated IL-4/IL-13 signaling contribute ...

CAMBRIDGE, Mass. - Wave Life Sciences Ltd . (NASDAQ:WVE), a clinical-stage biotechnology company with a market capitalization of $1.87 billion, has announced the commencement of its Phase 1 INLIGHT ...

Listen to this article The Virginia Home plans to build a $128 million, 75-acre campus in Hanover County, according to a Thursday announcement by the nonprofit, which serves adults with irreversible ...

Entrada plans to initiate clinical testing of ENTR-601-44 in Duchenne MD patients amenable to exon 44 skipping later this year.

Tony, from Skellingthorpe, Lincoln, was diagnosed with myofibrillar myositis and anti-SRP immune-mediated necrotizing ...

Columnist Betty Vertin has learned that as a parent, she's finding the years with all her children, including those with DMD, too short.

WVE-007 is a novel, long-acting GalNAc-siRNA targeting INHBE mRNA – a genetically validated target that provides a new approach for healthy, ...

Nonprofits that challenged to the Trump administration’s freezing of grant funds highlighted crisis for a small center in ...

usz.ch Background: Duchenne muscular dystrophy (DMD) leads to progressive impairment of ... dependence on care and respiratory impairment in patients with DMD from childhood to adult life is valuable ...

WVE-007 is a novel, long-acting GalNAc-siRNA targeting INHBE mRNA - a genetically validated target that provides a new approach for healthy, sustainable weight loss (fat loss with muscle preservation) ...

Shares of PTC Therapeutics, Inc. (NASDAQ:PTCT – Get Free Report) shot up 6.1% during trading on Monday after Cantor Fitzgerald raised their price target on the stock from $76.00 to $113.00. Cantor ...