Patient advocate Austin Leclaire, who died Feb. 1, played a pivotal role in spurring the development of the first medicines ...

Entrada plans to initiate clinical testing of ENTR-601-44 in Duchenne MD patients amenable to exon 44 skipping later this year.

Tony, from Skellingthorpe, Lincoln, was diagnosed with myofibrillar myositis and anti-SRP immune-mediated necrotizing ...

Contrary to prior data, this study shows that neither eosinophils nor STAT6-mediated IL-4/IL-13 signaling contribute ...

Columnist Betty Vertin has learned that as a parent, she's finding the years with all her children, including those with DMD, too short.