Patient advocate Austin Leclaire, who died Feb. 1, played a pivotal role in spurring the development of the first medicines ...

The symptoms of myotonic dystrophy may be obvious from birth or they can develop later -- during the teenage or adult years. Like other forms of muscular dystrophy, myotonic dystrophy leads to ...

Duchenne muscular dystrophy (DMD) is the most common type ... They should see a cardiologist in their late teens or early adult years to check for any problem. Some blood pressure medicines ...

In the case of limb-girdle muscular dystrophy, muscle deterioration is progressive and young adults lose the ability to walk and normal use of their arms and hands. "You go from being a good ...

Contrary to prior data, this study shows that neither eosinophils nor STAT6-mediated IL-4/IL-13 signaling contribute ...

Entrada plans to initiate clinical testing of ENTR-601-44 in Duchenne MD patients amenable to exon 44 skipping later this year.

Tony, from Skellingthorpe, Lincoln, was diagnosed with myofibrillar myositis and anti-SRP immune-mediated necrotizing ...