Cell and gene therapy (C&GT) is set to revolutionise treatment of complex diseases, offering new possibilities for patients.

The National University Centre for Organ Transplantation (NUCOT) has launched the inaugural Tree Planting Legacy Project, ...

From the outside, Savannah McKell, from NSW, seemed to have a picture-perfect life. But behind closed doors, the Newcastle ...

Spinraza (nusinersen) treatment helped school-age children with SMA be more independent in tasks involving their arms and ...

The Information Day takes place on Wednesday 4 June 2025, in Lisburn, Co. Antrim, and is organised by Muscular Dystrophy UK, the leading charity for more than ...

Roche presented promising 96-week data from the Phase II FENopta study, showing that its investigational drug, fenebrutinib, significantly reduce ...

Panelists discuss how supportive care for patients with spinal muscular atrophy (SMA) includes rehabilitation, respiratory ...

Columnist Alyssa Silva was hoping an MRI would clarify the medical mystery of her lower back pain, but it didn't work out ...