Three patients with spinal muscular atrophy had improved muscle strength and could walk farther after a month of daily spinal ...

HAILEY, Idaho (KMVT/KSVT) —February 29th is Rare Disease Day, one of the diseases that is being researched is Spinal Muscular Atrophy. It’s a disease that people are born with that affects ...

A Boston-area biopharmaceutical firm has submitted a biologics license application to the FDA for its investigational, fully ...

Nawai lost control of her muscles as a baby, when she was diagnosed with a rare genetic disease called Spinal Muscular Atrophy at three ... Nawai has outlived her life expectancy and has gotten ...