The scientists at the University of California, San Francisco, and Johns Hopkins University in Baltimore injected an ...

Evidence is mounting that clinicians can treat serious genetic disorders prenatally by injecting medicine into the amniotic ...

Injecting medicine into the amniotic fluid staves off progression of spinal muscular atrophy in utero.Evidence is mounting ...

Ridhay’s parents received the devastating diagnosis just months ago, and they’ve since been living each day with a renewed ...

Panelists discuss how the needs of older patients with spinal muscular atrophy (SMA) differ from infants, focusing on ...

Panelists discuss how spinal muscular atrophy (SMA) progresses over time, affecting motor function differently in older ...

A wearable robotic device called HAL improved walking ability for SMA patients who also received Spinraza (nusinersen), a ...