SMA is caused by a defect in the survivor motor neuron one gene ... one is called SMN 1 – that’s what’s missing in spinal muscular atrophy.” Now, the first FDA-approved oral medication ...

Spinal muscular atrophy is caused by mutations in the survival motor neurons gene, SMN1.The SMN protein localizes to both the cytoplasm and the nuclear bodies. One hallmark of spinal muscular ...

A Boston-area biopharmaceutical firm has submitted a biologics license application to the FDA for its investigational, fully ...

Three patients with spinal muscular atrophy had improved muscle strength and could walk farther after a month of daily spinal ...

A large, retrospective analysis of patients with amyotrophic lateral sclerosis (ALS) and progressive muscular atrophy ... upper motor neuron signs in the PMA patients was unrelated to survival ...

A new drug-free, minimally invasive intervention targets the root cause of progressive loss of neural function in spinal muscle atrophy (SMA), an inherited neuromuscular disease.

This is what happens to infants born with spinal muscular atrophy ... SMA is caused by a defect in the survival motor neuron ...

Electrical stimulation of the spinal cord strengthened the muscles of three people with spinal muscular atrophy, a rare motor neuron disease.

An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...

Biogen has announced that the European Medicines Agency (EMA) and US Food and Drug Administration (FDA) have started reviewing a higher dose regimen of its spinal muscular atrophy ... levels of the ...

Request To Download Free Sample of This Strategic Report @ Introduction Spinal Muscular Atrophy (SMA) is a rare genetic disorder characterized by the progressive loss of motor neurons, leading to ...

We are pleased to announce that our applications for the higher dose regimen of nusinersen are now under review in the US and Europe,” said Stephanie Fradette, Pharm.D., Head of the Neuromuscular ...