Nusinersen - Wikipedia
Nusinersen, [7] marketed as Spinraza, [4] is a medication used in treating spinal muscular atrophy (SMA), a rare neuromuscular disorder. [8] [4] In December 2016, it became the first approved drug used in treating this disorder.
Nusinersen (Spinraza®) – Spinal Muscular Atrophy (SMA)
Nusinersen, marketed in the U.S. as Spinraza ® (Biogen) is the first therapy approved for the treatment of SMA. SMA results from mutations in a gene known as SMN1, which encodes a protein (Survival Motor Neuron, or SMN) important for motor neuron survival.
Nusinersen injection Uses, Side Effects & Warnings - Drugs.com
Sep 12, 2024 · Nusinersen works by helping the body produce a protein essential to the function of nerves that control muscle movement. This protein is lacking in people with an inherited disorder called spinal muscular atrophy caused by a mutation in a specific gene.
Official Patient Site | SPINRAZA® (nusinersen)
SPINRAZA ® (nusinersen) is a prescription medicine used to treat spinal muscular atrophy (SMA) in pediatric and adult patients. Increased risk of bleeding complications has been observed after administration of similar medicines.
SPINRAZA (nusinersen) injection, for intrathecal use . Initial U.S. Approval: 2016 _____ INDICATIONS AND USAGE _____ and as clinically needed. SPINRAZA is a survival motor neuron-2 (SMN2)-directed antisense oligonucleotide indicated for the treatment of spinal muscular atrophy (SMA) in pediatric and adult patients (1)
Nusinersen (Spinraza) for Spinal Muscular Atrophy Treatment
One of the latest breakthroughs in care for patients with spinal muscular atrophy is the FDA approval of a new medicine called nusinersen (brand name Spinraza) for the treatment of SMA in children and adults.
Nusinersen Injection: MedlinePlus Drug Information
Nusinersen injection is used for the treatment of spinal muscular atrophy (an inherited condition that reduces muscle strength and movement) in infants, children, and adults. Nusinersen injection is in a class of medications called antisense oligonucleotide inhibitors.
How SPINRAZA® (nusinersen) Works
SPINRAZA ® (nusinersen) is a prescription medicine used to treat spinal muscular atrophy (SMA) in pediatric and adult patients.
SPINRAZA (nusinersen) injection, for intrathecal use Initial U.S. Approval: 2016 . INDICATIONS AND USAGE . SPINRAZA is a survival motor neuron-2 (SMN2)-directed antisense oligonucleotide...
Nusinersen: A Treatment for Spinal Muscular Atrophy
It is a novel modified antisense oligonucleotide designed to treat SMA caused by mutations in chromosome 5q that lead to survival motor neuron protein deficiency. Nusinersen has been studied for safety, pharmacokinetics, and efficacy in …